"gene therapy" 的定义和意义

What is "gene therapy"?

Gene therapy is a medical treatment that aims to treat or prevent diseases by changing the genetic structure of cells. It involves inserting genetic material into a person's cells to correct abnormal genes or provide new functions. Gene therapy can potentially replace missing or flawed genes, activate existing genes, or change how genes work in the body. This approach shows potential for treating inherited disorders like cystic fibrosis and certain types of cancer by addressing the underlying genetic causes.